Category Archives: ALS Treatment

New research makes a discovery that suggests a clear approach for developing a potential therapy for ALS. Continue reading →

To expedite positive patient outcomes, U.S. Sen. Martha McSally (R-AZ) on June 3 introduced a GOP-led bill that would establish a time-limited provisional approval pathway for certain drugs and biological products. Continue reading →

June 09, 2020 16:30 ET | Source: Denali Therapeutics Inc. SOUTH SAN FRANCISCO, June 09, 2020 (GLOBE NEWSWIRE) -- Denali Therapeutics Inc. (NASDAQ: DNLI), a biopharmaceutical company developing a broad portfolio of product candidates engineered to cross the blood-brain barrier (BBB) for neurodegenerative diseases, today announced the results from its Phase 1b studies with small molecule RIPK1 inhibitor DNL747 in Alzheimers disease and ALS, and provided a broad RIPK1 program update including DNL788 and DNL758. Continue reading →

A drug-addicted man wearing a protective face mask prepares a line of cocaine on his smartphone on ... [+] May 13, 2020, in a street of Lausanne, western Switzerland, amid the COVID-19 outbreak, caused by the novel coronavirus. Continue reading →

SALT LAKE CITY, May 26, 2020 /PRNewswire/ -- Clene Nanomedicine, Inc., a clinical-stage biopharmaceutical company, today announcedits Australian subsidiary has completed over 50% of participant randomization in the Phase 2 RESCUE-ALS study with its lead nanocatalytic therapy, CNM-Au8, for the treatment of Amyotrophic Lateral Sclerosis (ALS). Continue reading →

May 27, 2020 17:14 ET | Source: Affiliated Managers Group, Inc. WEST PALM BEACH, Fla., May 27, 2020 (GLOBE NEWSWIRE) -- Affiliated Managers Group, Inc. (NYSE: AMG), a global asset management company, today announced with sadness the passing of Sean M Continue reading →

European authorities must step up efforts to screen babies for a multitude of genetic disorders, a panel of experts suggested during a May 14-15 online medical conference. The session was part of the 10th European Conference on Rare Diseases & Orphan Products (ECRD2020) which was to have occurred in Stockholm, but instead took place online via Zoom. Were interested in this topic because our community feels poorly served by newborn screening, said Nick Meade, policy director at Genetic Alliance UK, a national charity representing more than 230 British patient advocacy organizations. Continue reading →

Orphazyme A/S Company announcement No. 34/2020 Company Registration No. Continue reading →

Pat Emery, a 1983 Elder High School graduate, was diagnosed with amyotrophic lateral sclerosis (ALS) in March during the novel coronavirus pandemic. Emery's friends and family have started a fundraising campaign to get Pat a wheelchair-accessible van so he can make it back to The Pit to see Elder play football this season.(Photo: Provided) Pat Emerys speech is a little labored these days. Short breaths break up his sentences, but the occasional pause pales in comparison to the passion and energy that still define his voice Continue reading →

Phil Green, Opinion contributor Published 6:30 a.m. MT May 21, 2020 ALS stands for amyotrophic lateral sclerosis, but is more commonly known as Lou Gehrig's disease. It's a neurodegerative disease that breaks down nerve cells in the brain and spinal cord, causing paralysis, according to the ALS Association website Continue reading →