Category Archives: Gene Therapy Trials

There has been much excitement over the announcements of results of the Gene Therapy trials conducted by Dr Robin Ali (fast becoming a hero in my world!). Read more from the original source: Gene Therapy Trials by Professor Robin Ali on German ZDF TV … Continue reading →

Professor Eric Alton from the UK CF Gene Therapy Consortium gives us a update on the gene therapy trials funded by the CF Trust. See the original post: Professor Eric Alton on the latest developments in gene therapy for cystic fibrosis … Continue reading →

There has been much excitement over the announcements of results of the Gene Therapy trials conducted by Dr Robin Ali (fast becoming a hero in my world!). The trial is for a treatment for LCA, Leber's Congenital Amaurosis, a rare form of a Retinal Disease / Retinitis Pigmentosa and has produced some amazing results. This video shows the before and after results of Steven navigating a darkened room with obstacles in his way. Read more here: First results of Gene Therapy Trials by Professor Robin Ali … Continue reading →