Category Archives: Muscular Dystrophy Treatment

Loma Linda University Childrens Hospital recently gave its first administration of a new gene replacement therapy to an infant who screened positive for spinal muscular atrophy (SMA), the top genetic killer of children under the age of two, potentially providing a symptom-free life for the patient. Childrens Hospital physicians said the new drug therapy, Zolgensma, is a revolution in neurological pediatric care Continue reading →

Market Report Summary For Full Information -> Click Here Read Full Press Release Below As per the report by Persistence Market Research (PMR), the globalduchenne muscular dystrophy marketis expected to experience strong growth. Continue reading →

November 02, 2020 01:00 ET | Source: Santhera Pharmaceuticals Holding AG multilang-release Pratteln, Switzerland, November2, 2020 Santhera Pharmaceuticals (SIX:SANN) provides a corporate update following implementation of an organizational restructuring and its move to a focus on vamorolone, a first-in-class dissociative steroid with a novel mode of action, to which the Company recently obtained global rights in all indications. Continue reading →

Market Report Summary For Full Information -> Click Here Read Full Press Release Below As per the report by Persistence Market Research (PMR), the globalduchenne muscular dystrophy marketis expected to experience strong growth. The market is also estimated to expand at a CAGR of 48.3% during the forecast period. The global duchenne muscular dystrophy market is estimated to bring in US$ 10,664.5 million revenue by the end of 2026. Continue reading →

A foundation started by a Manalapan couple raised $165,000 for research for a cure to a rare disease with a 260-mile walk earlier this month. JAR of Hope was created in 2013 by James and Karen Raffone when their son, James Anthony (Jamesy), was diagnosed with Duchenne Muscular Dystrophy at the age of four. There is no cure for the disease, which causes those it afflicts to be wheelchair-bound and then progresses to them being hooked up on ventilators before a young and tragic death Continue reading →

marketresearchhub Presents Duchenne Muscular Dystrophy Therapeutics Market Size, Status and Forecast 2020-2026 New Document to its Studies Database This report, which has been published, is having a meaningful Duchenne Muscular Dystrophy Therapeutics market insight. It casts some lights on industry products and services. Along with those product applications, it also examined whether it reaches up to the end-users or not Continue reading →

SOUTH PLAINFIELD, N.J., Oct. 29, 2020 /PRNewswire/ --PTC Therapeutics, Inc. Continue reading →

WIRED Health:Tech is one of the most prominent annual conferences exploring technological advances in medicine. Continue reading →

BOULDER, Colo.--(BUSINESS WIRE)--Edgewise Therapeutics, a clinical-stage biopharmaceutical company developing small molecule therapies for musculoskeletal diseases, today announced the appointment of John Moore to the newly created position of General Counsel. Mr. Continue reading →

The original is unfaithful to the translation, Jorge Luis Borges Investing in new innovative RNA technologies can lead to rapid value creation, and Europe is a fertile ground to hunt for them. Continue reading →